Orphan Drugs — Manufacturers, Suppliers & Exporters

PharmaTradz lists 42 Orphan Drugs products from verified GMP-certified manufacturers, suppliers and exporters worldwide, available as Tablets, Injection, Capsules, Oral Solution and more. Commonly sourced molecules include Lenalidomide 5 mg Capsule, Treprostinil IV, Deutivacaftor + Tezacaftor + Vanzacaftor. Buyers can compare specifications, request bulk quotes, and source with regulatory documentation (COA, GMP certificates, CTD/ACTD dossiers) for import into their market.

Products listed

Dosage forms

500+

Verified suppliers

100+

Countries served

Available dosage forms

Tablets (14) Injection (10) Capsules (7) Oral Solution (3) Capsules. (1) Intrathecal Injection (1) Injectable Solution (1) Inhalation Solution (Nebulizer) (1)

Reference brands in this category

Lenalid Bkemv Soliris Phyrago Jakafi Sutent Kyprolis Tasigna Talquetamide Pomalyst Caprelsa Rilutek

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Browse Orphan Drugs products

Agalsidase beta

Strength: 35 mg

Form: Injection

Reference Brands: Fabrazyme (USA/EU)

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Alglucosidase Alfa IV

Strength: 50 mg/vial

Form: Lyophilized powder

Reference Brands: Lumizyme®(US & EU)

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Ambrisentan tablets

Strength: 5 mg and 10 mg

Form: Tablets

Reference Brands: Letairis®(US & EU); Volibris®(EU)

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Arimoclomol

Strength: 47 mg, 62mg, 93mg

Form: Capsules

Reference Brands: MIPLYFFA (USA)

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Bosentan tablet

Strength: 62.5 mg and 125 mg

Form: Tablets

Reference Brands: Tracleer®(US & EU)

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Carfilzomib injection

Strength: 60mg/vial

Form: Injection

Reference Brands: Kyprolis

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Carglumic Acid

Strength: 200mg

Form: Dispersible Tablets

Reference Brands: Carbaglu (USA/EU)

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Dasatinib 100 mg Tablet

Strength: 100 mg, 20 mg

Form: Tablets

Reference Brands: Phyrago (USA)

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Deutivacaftor + Tezacaftor + Vanzacaftor

Strength: 10 mg + 50 mg + 125mg

Form: Tablets

Reference Brands: Alyftrek (USA)

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Doxecitine + Doxribtimine

Strength: 2g+2g

Form: Oral Solution

Reference Brands: Kygevvi (USA)

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Eculizumab 300 mg Injection

Strength: 300mg/30ml

Form: Injection

Reference Brands: Bkemv (USA), Soliris (EU/LATAM)

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Edaravone injection

Strength: 30 mg/10 ml

Form: Injectable Solution

Reference Brands: Radicava(US)

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Frequently asked questions about Orphan Drugs

PharmaTradz lists GMP-certified manufacturers, suppliers and exporters supplying Orphan Drugs products. Every supplier passes KYC business checks, and GMP certificates and export history are verified before a Verified mark appears on their profile.

Orphan Drugs products on PharmaTradz are available as Tablets, Injection, Capsules, Oral Solution, Capsules., Intrathecal Injection. Specific strengths and pack sizes are listed on each product page.

Open any product and click "Get Enquiry", or send an RFP describing the molecule, strength, destination market and quantity. PharmaTradz matches your requirement to verified suppliers able to serve that market and returns structured quotes.

Yes. Many listings include dossier availability in CTD, EU-CTD or ACTD format, with bioequivalence data where applicable. Dossier licensing and out-licensing opportunities can be requested through the same enquiry process.

Suppliers on PharmaTradz export to 100+ countries across Asia, Africa, Latin America, MENA, the EU and CIS. Share your destination market in the enquiry and we match suppliers with the right registrations and export experience. Controlled substances are supplied strictly against valid import and export permits.

Related therapeutic categories

Anemia Ayurvedic Herbal drugs Addiction Medicine / Substance Use Homeopathic Medicines Derma Drugs Hair Loss Neurology Pain Management

Orphan Drugs — Manufacturers, Suppliers & Exporters

Available dosage forms

Reference brands in this category