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Orphan Drugs

Trusted pharma products in Orphan Drugs

Ruxolitinib Tablet

Strength: 5mg, 15mg

Form: Tablets

Reference Brands: Jakafi

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Sapropterin Dihydrochloride tablet

Strength: 100 mg

Form: Tablets

Reference Brands: Kuvan®(US); Kuvanon®(EU)

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Sepiapterin

Strength: 1000 mg, 250 mg

Form: Tablets / oral powder

Reference Brands: Sephience (USA/EU)

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Sunitinib Malate Tablet

Strength: 25mg, 50mg

Form: Tablets

Reference Brands: Sutent (USA)

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Taliglucerase alfa

Strength: 200U

Form: Injection

Reference Brands: Elelyso (USA/EU)

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Tetrabenazine tablets

Strength: 25 mg, 50 mg, 75 mg

Form: Tablets

Reference Brands: Xenazine(US)

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Treprostinil IV or SC

Strength: 2 mg (0.1 mg/mL), 4 mg (0.2 mg/mL), 8 mg (0.4 mg/mL), 20 mg (1 mg/mL), 50 mg (2.5 mg/mL), 100 mg (5 mg/mL), 200 mg (10 mg/mL), or 400 mg (20 mg/mL)

Form: SC or Intravenous (IV)

Reference Brands: Remodulin®(US & EU)

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Trofinetide

Strength: 200 mg/mL

Form: Oral Solution

Reference Brands: Daybue (USA)

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Vandetanib Tablets

Strength: 300 mg

Form: Tablets

Reference Brands: Caprelsa

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Vutrisiran

Strength: 25mg/0.5ml

Form: Injection

Reference Brands: Amvuttra (USA/EU)

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